[Adrenal insufficiency as part of X-linked adrenoleukodystrophy].

Journal: Problemy endokrinologii
PMID:

Abstract

BACKGROUND:  X-linked adrenoleukodystrophy (X-ALD) is a severe neurodegenerative metabolic disease with a frequency 1:17,000 in newborn boys. Being a major part of X-ALD with an incidence of 70-80% of patients, adrenal insufficiency (AI) is a life-threatening condition without timely treatment. The possibility of developing AI during the whole disease duration and the absence of any predictive factor for AI joining shows the necessity of studying AI in X-ALD patients to optimize current diagnostic and treatment algorithms.

Authors

  • S R Enikeeva
    Endocrinology Research Centre.
  • I S Chugunov
    Endocrinology Research Centre.
  • M A Kareva
    Endocrinology Research Centre.
  • M V Kurkina
    Research Centre for Medical Genetics.
  • E Y Zakharova
    Research Centre for Medical Genetics.
  • S V Michailova
    Pirogov Russian National Research Medical University.
  • O B Bezlepkina
    Endocrinology Research Centre.
  • V A Peterkova
    Endocrinology Research Centre.
  • N G Mokrysheva
    Endocrinology Research Centre.