A machine learning model for early diagnosis of type 1 Gaucher disease using real-life data.

Journal: Journal of clinical epidemiology
Published Date:

Abstract

OBJECTIVE: The diagnosis of Gaucher disease (GD) presents a major challenge due to the high variability and low specificity of its clinical characteristics, along with limited physician awareness of the disease's early symptoms. Early and accurate diagnosis is important to enable effective treatment decisions, prevent unnecessary testing, and facilitate genetic counseling. This study aimed to develop a machine learning (ML) model for GD screening and GD early diagnosis based on real-world clinical data using the Maccabi Healthcare Services electronic database, which contains 20 years of longitudinal data on approximately 2.6 million patients.

Authors

  • Avraham Tenenbaum
    School of Medicine, Tel Aviv University, Tel Aviv, Israel.
  • Shoshana Revel-Vilk
    Gaucher Unit, The Eisenberg R&D Authority, Shaare Zedek Medical Center, Jerusalem, Israel; Faculty of Medicine, Hebrew University, Jerusalem, Israel; Braun School of Public Health and Community Medicine, Hebrew University, Jerusalem, Israel. Electronic address: srevelvilk@gmail.com.
  • Sivan Gazit
    MaccabiTech, Maccabi Healthcare Services, Tel Aviv, Israel.
  • Michael Roimi
    Department of Critical Care Medicine, Rambam Health Care Campus, Haifa, Israel.
  • Aidan Gill
    Takeda Pharmaceuticals International AG, Zurich, Switzerland.
  • Dafna Gilboa
    Takeda Israel Ltd, Petah Tikva, Israel.
  • Ora Paltiel
    Braun School of Public Health and Community Medicine, Hadassah-Hebrew University, Jerusalem, Israel.
  • Orly Manor
    Braun School of Public Health and Community Medicine, Hebrew University, Jerusalem, Israel.
  • Varda Shalev
    Institute of Health Research and Innovation, Maccabi Healthcare Services, Tel-Aviv, Israel.
  • Gabriel Chodick
    Maccabi Healthcare Services, Tel Aviv, Israel.